These medical breakthroughs and advances gave patients new hope in 2025

Notable results include a Huntington’s treatment and custom gene therapy

A smily chubby-cheeked baby is sitting in a rainbow striped cloth baby seat. His two sisters and brother sit around him. Everyone is smiling.

A gene therapy designed just for baby KJ Muldoon (center, surrounded by his siblings) saved his life.

CHOP

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American science took a beating this year, with cuts to funding, jobs and credibility.