Early-stage research could eventually lead to gene therapy
Borrowing a trick from nature, researchers have switched off the extra chromosome that causes Down syndrome in cells taken from patients with the condition.
Though not a cure, the technique, reported July 17 in Nature, has already produced insights into the disorder. In the long run it might even make the flaw that causes Down syndrome correctable through gene therapy.
“Gene therapy is now on the horizon,” says Elizabeth Fisher, a molecular geneticist