Gene Delivery: Mouse study shows new therapy may reverse muscular dystrophy

10:34am, August 4, 2004

For people with the most common type of muscular dystrophy, one faulty gene wreaks devastating consequences. Researchers have now found a way to deliver a working copy of the gene to the entire muscular system in mice that suffer from the muscle-wasting ailment. With one injection into the bloodstream, the animals' conditions improved markedly.

"No one's been able to get a delivery system to work very well before," says Jeffrey S. Chamberlain of the University of Washington in Seattle. "We were able to show a very significant effect in halting and reversing this disease."

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