For people with the most common type of muscular dystrophy, one faulty gene wreaks devastating consequences. Researchers have now found a way to deliver a working copy of the gene to the entire muscular system in mice that suffer from the muscle-wasting ailment. With one injection into the bloodstream, the animals' conditions improved markedly.
"No one's been able to get a delivery system to work very well before," says Jeffrey S. Chamberlain of the University of Washington in Seattle. "We were able to show a very significant effect in halting and reversing this disease."