Search Results for: GENE THERAPY
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1,053 results
1,053 results for: GENE THERAPY
- Genetics
Most of today’s gene therapies rely on viruses — and that’s a problem
The next big strides in gene therapy for rare diseases may come from CRISPR and new approaches to delivery.
- Health & Medicine
The first CRISPR therapy approved in the U.S. will treat sickle cell disease
In the world’s first CRISPR-based treatment, genetic tweaks to red blood cells aim to help people with the often debilitating disease.
- Genetics
Thomas Cech’s ‘The Catalyst’ spotlights RNA and its superpowers
Nobel Prize-winning biochemist Thomas Cech’s new book is part ode to RNA and part detailed history of the scientists who’ve studied it.
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- Genetics
The first gene therapy for muscular dystrophy has been approved for some kids
The U.S. Food and Drug Administration cleared a shortened version of a gene for a muscle protein to be used in 4- and 5-year-olds with muscular dystrophy.
- Health & Medicine
Early mRNA research that led to COVID-19 vaccines wins 2023 medicine Nobel Prize
Biochemists Katalin Karikó and Drew Weissman devised mRNA modifications to make vaccines that trigger good immune responses instead of harmful ones.
- Health & Medicine
Is aging without illness possible?
Researchers are harnessing basic biology to develop drugs that foster healthy aging. Just don’t call them antiaging pills.
- Health & Medicine
A gene editing technique shows promise for lowering LDL cholesterol
In a trial of 10 people with familial hypercholesterolemia, a genetic medicine reduced levels of LDL cholesterol in the blood by up to 55 percent.
- Health & Medicine
Fetuses make a protein that causes morning sickness in pregnancy
A hormone called GDF15 triggers a part of the brain involved in nausea and vomiting, a new study finds. Blocking its action may lead to treatments.
- Life
A gene therapy shot might keep cats from getting pregnant without being spayed
Even after mating with fertile males, females given the cat contraceptive, which targets an ovulation-preventing hormone, did not get pregnant.
- Health & Medicine
‘Dormant’ HIV has ongoing skirmishes with the body’s immune system
In people on HIV drugs, defective viral bits may still exhaust T cells, possibly making it harder to fight back if people go off the drugs.
- Genetics
50 years ago, scientists sequenced a gene for the first time
Within five decades, scientists went from sequencing a single gene to sequencing the entire human genome.
